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Andelyn Biosciences to Bring First Gene Therapy for Treatment of INAD to Clinical Trials

Infantile Neuroaxonal Dystrophy (INAD) is a rare inherited neurological disorder.

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By: Charlie Sternberg

Associate Editor

Andelyn Biosciences Inc., a patient-focused gene therapy Contract Development and Manufacturing Organization, will help the INADcure Foundation bring the first-ever gene therapy for the treatment of Infantile Neuroaxonal Dystrophy (INAD) to clinical trials.   Infantile Neuroaxonal Dystrophy (INAD) is a rare inherited neurological disorder caused by mutations in a gene called PLA2G6 that encodes for an enzyme known as Phospholipase A2. The disease leads to neurodegeneration in the nervous syste...

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